AGORA Gene Therapy
Facilitating access to effective gene therapies for treatment of patients with ultra-rare diseases in Europe
Who are we
We are an international group of physicians, scientists and patient advocacy and health policy experts working in the field of stem cell gene therapy for rare inherited immune diseases that aim to support and secure access to effective gene therapy treatment for patients cross borders
Learn more about our mission and vision
Latest news
AGORA Regulatory Workshop, Leiden January 16, 2024
This regulatory workshop on scientific alignment and regulatory convergence for innovative therapies for rare diseases brought together representatives from regulatory agencies in Europe, North America, Australia and Japan
AGORA meeting London September 22, 2022
This first AGORA multidisciplinary meeting brought together more than 50 stakeholders from across Europe, including researchers, funders, clinicians, regulatory agencies and industry partners. A report on this meeting was published in March 2023 as correspondence in Nature Medicine
